The genetic disease landed Yeo Wee Chong in the ICU, on a ventilator. He was just 29 then. Read more at straitstimes.com.

The FORTIS trial is investigating whether AT845, an adeno-associated virus (AAV) therapy, can deliver a functional copy of the acid alpha-glucosidase (GAA) gene directly in muscle cells in adults ...

People with this disease produce too little or no acid alpha-glucosidase (GAA), an enzyme that allows lysosomes to break glycogen down into usable glucose. Without GAA, glycogen deposits build up, ...

You take an alpha-glucosidase inhibitor with the first bite of each meal. Most people take a pill three times a day. An alpha-glucosidase inhibitor will usually lower your A1c (the "average" of ...