Riding recent momentum in the Duchenne muscular dystrophy space, Capricor Therapeutics, Wave Life Sciences, Regenxbio and ...

Duchenne muscular dystrophy (DMD) is a genetic condition that causes progressive muscle weakness and wasting. It is an X-linked recessive disorder that occurs due to changes in the DMD gene ...

Duchenne muscular dystrophy (DMD) is the most common type. It’s caused by flaws in the gene that controls how ... Scientists continue to look for new ways to treat DMD in clinical trials.

DMD is an X-linked recessive disorder, a genetic pattern that causes it to develop almost always in males. DMD is caused by ...

It’s a long protein with numerous redundant coils (purple balls), and acts like a shock absorber during ... muscle fibers are easily damaged. Duchenne muscular dystrophy results from mutations in the ...

Sarepta is pressing forward with a bold plan to file with the FDA for accelerated approval of its gene therapy SRP-9001 for Duchenne muscular dystrophy ... "We look forward to a collaborative ...

An experimental gene therapy for Duchenne muscular dystrophy has showed better-than-expected results in a three-patient trial, according to preliminary data presented by Cambridge, Massachusetts–based ...

Duchenne muscular dystrophy (DMD) is a rare genetic disorder that is characterised by progressive muscle degeneration and weakness, and is caused by mutations in the dystrophin gene. Currently ...

New data on Sarepta's gene therapy for Duchenne muscular dystrophy (DMD ... Sarepta's gene therapy – like rivals from Pfizer and Solid Biosciences – codes for a shortened form of the ...