Washington — U.S. health regulators on Tuesday approved the first gene therapy for ... which primarily affects men. Currently, patients receive frequent, expensive IVs of a protein that helps ...

Gene therapies are notoriously expensive, too—and, Mendell noted, there's no reason to think the treatments couldn't work together. "Both treatments have their benefits, and I think the ...

But the treatment’s hefty price tag makes it the most expensive drug in the world. And although it seems to be effective, gene-replacement therapies for the most common form of haemophilia ...

It's not a perfect test. Yet researchers report a key step for the first gene test aimed at reducing unnecessary angiograms — expensive and somewhat risky procedures that hundreds of thousands ...

A shot of Zolgensma, a gene therapy for spinal-muscular atrophy, comes to $2.1m. It is one of a new generation of ultra-expensive medicines. Treatments for beta-thalassemia and haemophilia ...

the most expensive medicine sold in the U.S., ranked by sticker price. But Spark CEO Jeff Marrazzo says Luxturna’s ability to restore vision in a small number of people with a defective gene ...