However, therapeutic agents can be delivered directly to the ... scientists can study how the function of the corresponding gene product (protein) is altered. With this information in hand ...

For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that ...

A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...

The preclinical data generated by agents produced by the GLP practice can be valuable in the later development of clinical trials in gene therapy. To help investigators choose the optimum vector ...

For recurrent respiratory papillomatosis (RRP), novel gene therapy to jump-start immunity to the human papillomavirus (HPV) ...

The California Institute for Regenerative Medicine has awarded a $6 million grant to USC investigators pioneering a new first ...

Cytoreductive gene therapy: to deliver an exogenous gene that causes cell death or allows the application of toxic agents. Immunomodulatory gene therapy: to induce gene expression that enhances ...

The study revealed multiple "common" and "cell specific" changes caused by insulin-resistance representing new targets for pharmacological or targeted gene therapy approaches. Richard Coward ...

Scientists looked at multiple techniques used to measure the modified viruses deployed in some gene therapy research and treatments. One technique, known as SEC-MALS, was the most precise and ...