Duchenne muscular dystrophy (DMD) is a rare hereditary disease that is associated with progressive muscle wasting. The ...
Managed Healthcare Executive provides C-suite executives at health plans and provider organizations with news, analysis, ...
Utrophin increase in muscle cells after transcriptional adaptation normalises cell function in Duchenne muscular dystrophy ...
For the small number of DMD patients with a gene mutation that can be treated by skipping exon 45 (a certain section of genetic code), doctors can prescribe the injectable drug casimersen (Amondys ...
The FDA is requiring Sarepta to perform a further clinical trial to prove that the drug improves motor function in DMD patients who have a particular mutation in a gene that produces dystrophin ...
Duchenne muscular dystrophy (DMD) is a rare genetic disorder that is characterised by progressive muscle degeneration and weakness, and is caused by mutations in the dystrophin gene. Currently ...
Results show improved functional outcomes for people with Duchenne muscular dystrophy who are ambulatory. Elevidys, which is ...
The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...
Duchenne muscular dystrophy occurs when that gene fails to make dystrophin. Becker muscular dystrophy occurs when a different mutation in the same gene results in some dystrophin, but it's either ...