Four-year-old Abby suffers regression in development due to Rett syndrome. Read more at straitstimes.com. Read more at ...

Neurogene said it would conduct daily monitoring for the "three Fs" in the week after dosing with the gene therapy.

After a patient died following a high dose of Neurogene’s Rett syndrome gene therapy candidate, the biotech is sharing ...

Taking center stage at the American Society of Gene and Cell Therapy meeting was the first-ever reported case of a ...

Treatment with trofinetide is tied to improvements in caregiver-reported outcomes by 9 months in individuals with Rett syndrome.

Neurogene has halted patient enrolment in the high-dose arm of its trial of Rett syndrome gene therapy, sparking another run on its shares. Last week, the company reported that NGN-401 had shown ...

For parents of children with Rett syndrome – a rare neurodevelopmental disorder that makes daily life challenging – it’s the small moments that bring the most joy. Although 14-year-old ...

Three Abstracts Accepted for Oral Presentations at 2025 International Rett Syndrome Foundation (IRSF) Rett Syndrome ...