So there are a, um, number of types in regard to SMA. Um, there are four types. And it based upon, the types of SMA are characterized by your motor development, meaning that how much strength do ...

The mutation that causes Spinal Muscular Atrophy (SMA) can be detected in a ... For example, children with a moderate phenotype (type II SMA) typically need mobility assistance at some point ...

More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...

One such condition is Spinal Muscular Atrophy (SMA), a genetic disorder affecting ... Symptoms of SMA can vary widely depending on the specific type and the age of onset. The most prevalent ...

in patients aged 2 to less than 18 years with spinal muscular atrophy (SMA) type 2. The randomized, double-blind, sham-controlled phase 3 STEER study (ClinicalTrials.gov Identifier: NCT05089656 ...

cells from the fibroblasts of a patient with spinal muscular atrophy (SMA), an inherited disorder in which mutations in the SMN1 gene cause selective loss of lower motor neurons, and lead to death ...

Back to Healio Topline results from a phase 3 clinical trial showed an investigational gene therapy for young people with spinal muscular atrophy type 2 increased mobility and slowed disease ...