More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...

DIAGNOSING: Diagnosing spinal muscular atrophy involves a combination of clinical evaluation, genetic testing, and sometimes additional diagnostic procedures. Given that SMA is a genetic disorder ...

The Amsterdam-based biotech firm said that its melt curve analysis-based test is used as a first-tier genetic screening tool to aid the diagnosis of SMA.

Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for Priority Review to be given. Explore more details here.

A man with a muscle-wasting disease is pleased Manitoba is asking a federal agency to reconsider its opposition to a ...

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...

For children with SMA, assistive devices -- walkers, wheelchairs, standers, and more -- are the key to staying active. Learn which ones may help your child.

Analytics company GlobalData has shared its optimism regarding the future of Novartis’ spinal muscular atrophy (SMA ... met its primary endpoint when testing the intrathecal formulation of ...

In a good-news-bad-news week for Biogen, the company will cut an undisclosed number of employees, just as a higher dose of ...

An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...

One such condition is Spinal Muscular Atrophy (SMA), a genetic disorder affecting infants and young children, impacting their movement and muscle function. SMA is a genetic disorder of movement ...

Health activists and patients with spinal muscular atrophy (SMA) have refuted the Central government’s affidavit in the Kerala High Court and demanded urgent action to reduce the cost of ...