Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for ...

Pharma: Launch of Shortages Monitoring Platform, several Changes re Clinical Trial Management in EU Countries; Devices: Resolution on the need ...

A group of Estonian psychiatrists and civic activists believe that allowing the therapeutic use of currently prohibited ...

Acadia Pharmaceuticals Inc. (Nasdaq: ACAD) today announced that the company has submitted a Marketing Authorization Application (MAA) to the European Medicines Agency (EMA) for trofinetide for the ...

Acadia Pharma seeks European marketing approval for trofinetide for the treatment of Rett syndrome: San Diego Thursday, January 16, 2025, 13:00 Hrs [IST] Acadia Pharmaceuticals In ...

Once identified, there is also the challenge of the geographic spread of individuals living with the same rare disease and then finding a means to ensure that each person can reach the clinical ...

Vladimir Putin’s forces are focusing on attacking on the outskirts of a key eastern Ukrainian city of Pokrovsk amid reports ...

was approved by the Medicines and Healthcare products Regulatory Agency (MHRA) as a treatment for moderately to severely active UC, a few weeks after it was cleared by the European Commission.

A key theme in this research is the role of ... Lastly, the interaction of experts within the European Medicines Agency illustrates the balance between supranational regulatory needs and national ...

Putin’s forces claim capture of strategic town as Zelensky makes Trump appeal - Separate Mechanised Brigade confirms ...

to the European Medicines Agency (EMA) for trofinetide for the treatment of Rett syndrome in adults and pediatric patients two years of age and older. If granted marketing authorization, trofinetide ...

Improved analytical techniques mean tiny amounts of endocrine disrupting compounds or PFAS can be found in many places. But is it a problem? Anthony King talks to the scientists on both sides of the f ...