New gene therapies could transform sickle cell treatment forever. A future without pain crises or hospitalizations may finally be within reach.

NHS approves £1.65m gene therapy for sickle cell disease, offering a potential cure. A milestone for patients, especially in ...

Jan. 17, 2025 — A new study has found older-looking brains in adults with sickle cell disease, helping to explain the cognitive challenges experienced by such individuals. A brain image from a ...

A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...

The new gene therapies for sickle cell disease—including the gene-editing treatment Casgevy, based on research at Boston Children's Hospital—have been game-changing for the patients who have ...

Individuals with SCT have one copy of the gene associated with sickle cell disease (SCD). SCD is a blood disorder characterized by misshapen blood cells that can cause blockages, leading to ...

Sickle cell anaemia is a genetic blood disorder characterised by the production of an abnormal haemoglobin, known as haemoglobin S. Sickle cell disease changes the shape of blood cells into a crescent ...

Dr. Kalen N. Wright (Emergency Medicine): A 21-year-old man with sickle cell disease was evaluated in the emergency department of this hospital after loss of consciousness resulting in a fall.

The chronic nature of Sickle Cell Disease and its impact on various organs can certainly drain money from one’s pocket or bank account over time. Since SCD affects multiple organs, the financial ...

A sickle cell disease “cure” is to be offered to NHS patients for the first time. The £1.65 million gene therapy called exa-cel, also known under the brand name Casgevy, uses a Nobel Prize ...

What would it look like to have a successful stem cell transplant? Would it be a cure for my sickle cell disease? It was a decision I could think about making because my sister was a genetic match ...