NDTV16d
Spinal Muscular Atrophy Sma
In a LinkedIn post, Monisha shared the challenges of travelling with her 14-year-old daughter, Keya, who has Spinal Muscular Atrophy (SMA). Understanding the early signs, potential complications ...
Healio8d
FDA receives biologics license application for apitegromab in spinal muscular atrophy
Scholar Rock, a Boston-area biopharma company, announced the submission of a biologics license application and request of priority review for apitegromab to treat spinal muscular atrophy.
GEN6d
Spinal Cord Stimulation Improves Leg Strength and Walking in Adults with SMA
minimally invasive intervention targets the root cause of progressive loss of neural function in patients with spinal muscular atrophy (SMA), an inherited neuromuscular disease. The pilot trial in ...
WebMD26d
Evrysdi for Spinal Muscular Atrophy: What You Need to Know
Evrysdi, also known as risdiplam, is an oral medicine used to treat spinal muscular atrophy (SMA) in children and adults. SMA is a genetic disease that is passed down through families.
WebMD26d
Spinraza for Spinal Muscular Atrophy: What You Need to Know
Spinraza, also known as nusinersen, is a medicine used to treat spinal muscular atrophy (SMA) in children and adults. SMA is a genetic disease that is passed down through families. It leads to ...
CBC.ca20d
Man with degenerative disease pleads for Manitoba to cover treatment while it asks drug agency to review
Jeremy Bray, who has Type 2 spinal muscular atrophy — a rare degenerative disease that has gradually robbed him of the ability to move his muscles — says he cannot wait for Canada's Drug ...
contemporarypediatrics8d
Apitegromab BLA submitted to FDA for spinal muscular atrophy
Scholar Rock has submitted a biologics license application (BLA) to the FDA for apitegromab, an investigational muscle-targeted therapy, for the treatment of spinal muscular atrophy (SMA). The ...
healthday6d
Spinal Zap Implant Helps Muscle Disease Patients Regain Strength
WEDNESDAY, Feb. 5, 2025 (HealthDay News) -- A new spinal cord implant may help people with spinal muscular atrophy (SMA) regain some muscle function, giving them stronger movement and improved walking ...
clinicaltrialsarena29d
Broader population could benefit from Novartis spinal muscular atrophy treatment
Credit: Taljat David / Shutterstock. Analytics company GlobalData has shared its optimism regarding the future of Novartis’ spinal muscular atrophy (SMA) gene transfer therapy – onasemnogene ...
KCBX5d
Spinal stimulation restored muscles wasted by rare genetic disorder
Daily electrical stimulation of certain nerves in the spinal cord appeared to help three people with spinal muscular atrophy (SMA), an inherited disorder that causes muscles to waste away. The ...
Associated Press6d
A spine-zapping implant helped 3 people with a muscle-wasting disease walk better
This image from video provided by UPMC and University of Pittsburgh Health Sciences shows Doug McCullough, who has spinal muscular atrophy, during tests of experimental spinal cord stimulation to ...