The FDA has extended the review period for the New Drug Application for elamipretide for the treatment of Barth syndrome.

how to correct it", says Barth. "Neurogenerative diseases for example can be the result of misregulated genes during early stages of pregnancy. In fact, there are a couple of severe diseases, such as ...

A new study finds that female individuals are less likely to be diagnosed with the syndrome, take longer to receive a diagnosis and are older when they are diagnosed than male individuals.

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Rett syndrome is a severe and complex neurodevelopmental disorder. Trofinetide, a synthetic analog of the N-terminal tripeptide of insulin-like growth factor 1 or IGF-1, is already approved in the ...

Quoin Pharmaceuticals (QNRX) announces interim clinical data from its ongoing Investigator Pediatric Netherton Syndrome clinical study. The Investigator Pediatric Study continues to demonstrate ...

Last month, media reports claimed that the accelerated accumulation of space debris had raised the real possibility of a "collision cascading" effect called the Kessler Syndrome. Kessler Syndrome ...

THE holiday season in the Philippines has been about reunions and feast. However, this has led to the rise of holiday heart syndrome, caused by excessive consumption of alcohol, stress, lack of rest, ...

Kessler Syndrome is a hypothetical scenario proposed by NASA scientist Donald J. Kessler in 1978 which predicts that when the density of objects in low Earth orbit (LEO)-roughly 100-1,200 miles ...

Elamipretide hydrochloride is under clinical development by Stealth BioTherapeutics and currently in Pre-Registration for Barth Syndrome. According to GlobalData, Pre-Registration drugs for Barth ...

Mets starting pitcher Shaun Marcum is out for the season due to thoracic outlet syndrome. He'll undergo surgery Monday to repair the issue, reports Jon Heyman of CBSSports.com. Marcum, 31 ...