Duchenne muscular dystrophy (DMD) is a rare hereditary disease that is associated with progressive muscle wasting. The ...

Riding recent momentum in the Duchenne muscular dystrophy space, Capricor Therapeutics, Wave Life Sciences, Regenxbio and ...

Duchenne muscular dystrophy (DMD) is the most common type. It’s caused by flaws in the gene that controls how ... Scientists continue to look for new ways to treat DMD in clinical trials.

Duchenne muscular dystrophy (DMD) is a genetic condition that causes progressive muscle weakness and wasting. It is an X-linked recessive disorder that occurs due to changes in the DMD gene ...

It’s a long protein with numerous redundant coils (purple balls), and acts like a shock absorber during ... muscle fibers are easily damaged. Duchenne muscular dystrophy results from mutations in the ...

Sarepta is pressing forward with a bold plan to file with the FDA for accelerated approval of its gene therapy SRP-9001 for Duchenne muscular dystrophy ... "We look forward to a collaborative ...

Duchenne muscular dystrophy (DMD) is a rare genetic disorder that is characterised by progressive muscle degeneration and weakness, and is caused by mutations in the dystrophin gene. Currently ...

A Phase 3 clinical trial investigating Elevidys (delandistrogene moxeparvovec), a gene therapy for Duchenne muscular dystrophy ... treatments work, they look like the high price of curing a ...

New data on Sarepta's gene therapy for Duchenne muscular dystrophy (DMD ... Sarepta's gene therapy – like rivals from Pfizer and Solid Biosciences – codes for a shortened form of the ...