Gene therapy may be 'one-shot stop' for rare bone disease
For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that ...
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New gene therapy shows promise for lifelong treatment of hypophosphatasia
For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that must be delivered by injection three-to-six times each week.
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USC receives $6 million grant for pioneering glioblastoma gene therapy
The California Institute for Regenerative Medicine has awarded a $6 million grant to USC investigators pioneering a new first ...
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Spur Therapeutics, FDA Align on Phase III Plans for Gaucher Disease Gene Therapy
The FDA has offered positive feedback on possible paths forward for accelerated or traditional approval of FLT201 using data from a single-arm study.
Microscopy approach offers new way to study cancer therapeutics at single-cell level
Understanding how tumors change their metabolism to resist treatments is a growing focus in cancer research. As cancer cells adapt to therapies, their metabolism often shifts, which can help them ...
Science Daily12h
Computer model helps identify cancer-fighting immune cells key to immunotherapy
Researchers have developed a computer model to help scientists identify tumor-fighting immune cells in patients with lung cancer treated with immune checkpoint inhibitors.