Exagamglogene autotemcel (exa-cel) gene therapy offers a potential cure for severe sickle cell disease, now available on NHS.

A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...

The new gene therapies for sickle cell disease—including the gene-editing treatment Casgevy, based on research at Boston Children's Hospital—have been game-changing for the patients who have ...

This article is part of a Health Affairs Forefront series on “The Future of Sickle Cell Disease Research and Care” with support from The American Society of Hematology. The articles in the ...

Individuals with SCT have one copy of the gene associated with sickle cell disease (SCD). SCD is a blood disorder characterized by misshapen blood cells that can cause blockages, leading to ...

The chronic nature of Sickle Cell Disease and its impact on various organs can certainly drain money from one’s pocket or bank account over time. Since SCD affects multiple organs, the financial ...

What would it look like to have a successful stem cell transplant? Would it be a cure for my sickle cell disease? It was a decision I could think about making because my sister was a genetic match ...

A sickle cell disease “cure” is to be offered to NHS patients for the first time. The £1.65 million gene therapy called exa-cel, also known under the brand name Casgevy, uses a Nobel Prize ...