Sidra Medicine Establishes Gene Therapy Centre For Rare Paediatric Diseases
Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...
Cherai residents rallying to support toddler’s battle against rare disease
KOCHI: Residents of Cherai are rallying to support two-and-a-half-year-old Adharv, who is suffering from Spinal Muscular ...
health.economictimes.indiatimes5d
Kerala to launch rare disease patient registry and treatment clinic
Thiruvananthapuram, A registry for rare disease patients in the state will become a reality this year, State Health Minister ...
Qatar Tribune on MSN1d
Qatar: Sidra establishes Gene Therapy Center for rare genetic diseases
The announcement was made at Arab Health 2025 where Sidra Medicine will highlight its international patient service programmes ...
The Week6d
Spinal muscular atrophy: Patients, activists seek health ministry’s intervention to bring down medicine cost
The health activists argue that the government is empowered with effective law and policy tools and therefore should ...
People with spinal muscular atrophy demand urgent action from the Centre to reduce medicine costs
Health activists demand government action to reduce the cost of SMA medicines, citing constitutional obligations and ...
PMLiVE1d
Biogen’s higher dose spinal muscular atrophy regimen accepted for review by EMA/FDA
Biogen has announced that the European Medicines Agency (EMA) and US Food and Drug Administration (FDA) have started ...
Pharm Exec6d
Biogen Seeks FDA Approval for a Higher Dosing Regimen of Spinraza for Spinal Muscular Atrophy
Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...
Daily4d
Rare Disease Patient Registry, Treatment Clinic soon in Kerala
Thiruvananthapuram: The Kerala government is planning to launch a registry for rare diseases and set up a treatment clinic in ...
Pharmabiz6d
Centre abdicates its constitutional obligation, criticises patients and experts on SMA issue
Centre abdicates its constitutional obligation, criticises patients and experts on SMA issue: Our Bureau, New Delhi Friday, January 24, 2025, 18:15 Hrs [IST] Patients and public h ...