Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists at St. Jude ...

The U.S. Food and Drug Administration has approved a new drug application for a tablet version of Evrysdi (risdiplam) for ...

On this episode, an infant with a harrowing diagnosis defies all odds after receiving a $2 million genetic treatment. Then, a ...

Scientists report results from a promising new approach to treat the rare neurodegenerative disorder. Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before ...

A girl on Long Island is speaking out after a clinical trial for Spinal Muscular Atrophy was cut by President Trump ...

Opens in a new tab or window Share on LinkedIn. Opens in a new tab or window The first prenatal treatment for spinal muscular atrophy showed promise in a single case report. Risdiplam was given to ...

Hi friends! Shane here! I just wanted to quick put up some reflections on my day today. I got my 7th Spinraza injection and ...

Exercise can make a significant difference for patients with SMA by working alongside other medical advancements to improve their quality of life. As a child, Mitchell Choma rarely sat still.

Researchers from Tokyo Metropolitan University have developed a way to treat aging-related muscular atrophy using regenerative medicine. Conventional methods to implant myoblasts, precursors to ...

Spinal muscle atrophyorspinal muscular atrophy(SMA) is a genetic disorder that can affect babies, children, and adults. A ...

Comprehensive intervention involving exercise, nutrition, and pharmacological therapy may be warranted for managing muscular atrophy in COPD. Muscular atrophy in patients with chronic obstructive ...