Cystic Fibrosis News Today Home | Cystic Fibrosis News Today
Dec 13, 2024 · Becoming educated and informed about cystic fibrosis is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
Cystic Fibrosis News -- ScienceDaily
Jun 11, 2024 · May 24, 2022 — Cystic fibrosis is a rare genetic disease which can cause very serious symptoms. In particular, patients suffer from chronic bacterial infections that can lead to respiratory...
FDA approves new breakthrough therapy for cystic fibrosis
FDA approves breakthrough therapy Trikafta for patients 12 and older with cystic fibrosis who have at least one F508del mutation in the CFTR gene, estimated to represent 90% of the cystic...
News - Cystic Fibrosis Foundation
Through grants, advocacy, and the development of a consensus guideline, the Cystic Fibrosis Foundation continues to advance its Newborn Screening Initiative, pushing for better newborn screening practices to curb delayed diagnoses and further progress health equity.
The Cystic-Fibrosis Breakthrough That Changed Everything
Mar 7, 2024 · A new age of American anti-Semitism, a breakthrough cystic-fibrosis treatment, Jodie Foster, and a "secret" Gospel.
FDA Approves New, Once-a-Day CFTR Modulator for People With CF | Cystic ...
Dec 20, 2024 · “We are excited that there is another treatment option for people with cystic fibrosis, especially for those who previously weren’t eligible for a modulator,” said JP Clancy, MD, senior vice president of clinical research for the Cystic Fibrosis Foundation. ... Recent news FDA Approves Trikafta for 94 Additional Rare CFTR Mutations . News ...
FDA Approves Trikafta for 94 Additional Rare CFTR Mutations
Dec 20, 2024 · The approval enables a small number of people with cystic fibrosis in the U.S. who were not previously eligible for a CFTR modulator therapy to access a drug that treats the underlying cause of their disease for the first time.. The FDA based its decision on laboratory evidence submitted by Vertex Pharmaceuticals that demonstrates these CFTR mutations respond to Trikafta and on established ...
6 months of Kaftrio treatment found to reduce inflammation in CF
Dec 20, 2023 · In people with cystic fibrosis (CF), six months of treatment with Kaftrio — sold as Trikafta in the U.S. — significantly reduced the blood levels of molecules called chemokines that are involved in inflammation, new research shows.
Phase 3 trials of new triple-combo CFTR modulator to report results
Jan 10, 2024 · Results of three global clinical trials of a new triple-combination CFTR modulator therapy for cystic fibrosis (CF) — vanzacaftor, tezacaftor and deutivacaftor — are expected shortly, Vertex Pharmaceuticals, the therapy’s developer, announced.
Cystic fibrosis - BBC News
Aug 4, 2024 · A man whose brother died waiting on a double lung transplant says more work is needed to make Cystic Fibrosis drugs available.